Enrollment is complete for the first groups of sickle cell patients taking pociredir and enrollment has begun for the 20 mg ...

On Thursday, the agency announced that it plans to recruit one million new donors over the next five years, citing a ...

A gene therapy recently approved by the FDA to treat patients with Sickle Cell Anemia is now being administered in St. Louis.

In her new book about overcoming life’s obstacles, Salintae Tuzo-Smith writes that whatever your struggles, you are more ...

Vertex Pharma's £1.65 million ($2.05 million) gene-editing therapy for sickle cell disease (SCD ... painful attacks that occur when red blood cells become misshapen and block blood vessels ...

CRISPR Therapeutics, whose CEO is Samarth Kulkarni, and Vertex Pharmaceuticals earned the first U.S. Food and Drug ...

Beam Therapeutics and Verve Therapeutics have each built their lead candidates on a technique billed as a safer alternative ...

Good morning and Welcome to Fulcrum Therapeutics first quarter 2025 financial results and business update conference call. (Operator Instructions). This call is being webcast live and can be accessed ...

In August 2022, the US Food and Drug Administration (FDA) approved the first gene therapy for transfusion-dependent ...

Apr. 11, 2025 — A multi-institutional team developed a chimeric antigen receptor (CAR) T cell-based ... cancer stem cells that seed cancer relapses, ... Feb. 27, 2025 — Red blood cells carry ...