A child with hereditary deafness regained their hearing thanks to a successful gene therapy surgery. 11-year-old Aissam Dam became the first person to get gene therapy in the United States for ...

Find out if gene therapy has also find its way into skin diseases. With two approvals in the last 2 years, is it the start of ...

The new soundwave-based treatment shows promise in stopping the growth of harmful brain lesions, without surgery or ...

Shortly after being born during the summer of 2024, KJ Muldoon was diagnosed with severe Carbamoyl Phosphate Synthetase 1 ...