CRISPR–Cas9-based therapies are widely investigated for their clinical applications. However, there are limitations ...
Genetic disorders occur due to alterations in the primary genetic material—deoxyribonucleic acid (DNA)—of an organism.
TEK IMAGE/Science Photo Library / Getty Images/Science Photo Libra A single infusion of an experimental gene-editing drug appears safe and effective for cutting cholesterol, possibly for life, ...
The Phase 1/2 trial is a first-in-human, open-label, multi-national study designed to evaluate the safety, tolerability, and efficacy of TSRA-196 in adults with AATD. Trial participants will receive a ...
The need to change regulations around gene-editing treatments was endorsed in November by the head of the US Food and Drug ...
A patient death in a CRISPR trial halts gene editing studies, raising critical safety questions. What this means for the ...
The study used large-scale CRISPR gene-editing technology to systematically determine which genes are required as embryonic ...
A baby born with a rare and dangerous genetic disease is growing and thriving after getting an experimental gene editing treatment made just for him. Researchers described the case in a new study, ...
A single infusion of an experimental gene-editing drug appears safe and effective for cutting cholesterol, possibly for life, according to a small early study released Saturday. The study, which ...
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